Table Of Contents

1. Introduction

1.1 Market Definition

1.2 Scope (Inclusion and Exclusions)

1.3 Research Assumptions

2. Executive Summary

2.1 Market Overview

2.2 Regional Synopsis

2.3 Competitive Summary

3. Research Methodology

3.1 Top-Down Approach

3.2 Bottom-up Approach

3.3. Data Validation

3.4 Primary Interviews

4. Market Dynamics Impact Analysis

4.1 Market Driving Factors Analysis

4.1.1 Drivers

4.1.2 Restraints

4.1.3 Opportunities

4.1.4 Challenges

4.2 PESTLE Analysis

4.3 Porter’s Five Forces Model

5. Statistical Insights and Trends Reporting

5.1 Disease Incidence and Prevalence (2024)

5.2 Clinical Trial Activity & Regulatory Approvals (2024), by Region

5.3 Vector Platform Adoption Rate, by Region (2020–2032)

5.4 Gene Therapy R&D Investment, by Region (Government, Commercial, VC/Private), 2024

6. Competitive Landscape

6.1 List of Major Companies by Region

6.2 Market Share Analysis by Region

6.3 Product Benchmarking

6.3.1 Product specifications and features

6.3.2 Pricing

6.4 Strategic Initiatives

6.4.1 Marketing and promotional activities

6.4.2 Distribution and Supply Chain Strategies

6.4.3 Expansion plans and new product launches

6.4.4 Strategic partnerships and collaborations

6.5 Technological Advancements

6.6 Market Positioning and Branding

7. Gene Therapy Platform Market Segmentation By Type

7.1 Chapter Overview

7.2 Viral Vector Platforms

7.2.1 Viral Vector Platforms Market Trends Analysis (2021-2032)

7.2.2 Viral Vector Platforms Market Size Estimates and Forecasts to 2032 (USD Billion)

7.3 Non-Viral Vector Platforms

7.3.1 Non-Viral Vector Platforms Market Trends Analysis (2021-2032)

7.3.2 Non-Viral Vector Platforms Market Size Estimates and Forecasts to 2032 (USD Billion)

7.4 Gene Editing Platforms

7.4.1 Gene Editing Platforms Market Trends Analysis (2021-2032)

7.4.2 Gene Editing Platforms Market Size Estimates and Forecasts to 2032 (USD Billion)

8. Gene Therapy Platform Market Segmentation By Application

8.1 Chapter Overview

8.2 Oncology

8.2.1 Oncology Market Trends Analysis (2021-2032)

8.2.2 Oncology Market Size Estimates and Forecasts to 2032 (USD Billion)

8.3 Rare Genetic Disorders

         8.3.1 Rare Genetic Disorders Market Trends Analysis (2021-2032)

8.3.2 Rare Genetic Disorders Market Size Estimates and Forecasts to 2032 (USD Billion)

8.4 Cardiovascular Diseases

         8.4.1 Cardiovascular Diseases Market Trends Analysis (2021-2032)

8.4.2 Cardiovascular Diseases Market Size Estimates and Forecasts to 2032 (USD Billion)

8.5 Neurological Disorders

         8.5.1 Neurological Disorders Market Trends Analysis (2021-2032)

8.5.2 Neurological Disorders Market Size Estimates and Forecasts To 2032 (USD Billion)

8.6 Ophthalmic Diseases

         8.6.1 Ophthalmic Diseases Market Trends Analysis (2021-2032)

8.6.2 Ophthalmic Diseases Market Size Estimates and Forecasts To 2032 (USD Billion)

8.7 Hematological Disorders (e.g., Hemophilia, Sickle Cell)

         8.6.1 Hematological Disorders (e.g., Hemophilia, Sickle Cell) Market Trends Analysis (2021-2032)

8.6.2 Hematological Disorders (e.g., Hemophilia, Sickle Cell) Market Size Estimates and Forecasts To 2032 (USD Billion)

8.8 Musculoskeletal Disorders

         8.8.1 Musculoskeletal Disorders Market Trends Analysis (2021-2032)

8.8.2 Musculoskeletal Disorders Market Size Estimates and Forecasts To 2032 (USD Billion)

8.9 Infectious Diseases (e.g., HIV, COVID-19 adjunct therapies)

         8.9.1 Infectious Diseases (e.g., HIV, COVID-19 adjunct therapies) Market Trends Analysis (2021-2032)

8.9.2 Infectious Diseases (e.g., HIV, COVID-19 adjunct therapies) Market Size Estimates and Forecasts To 2032 (USD Billion)

9. Gene Therapy Platform Market Segmentation By Delivery Mode

9.1 Chapter Overview

9.2 In Vivo Gene Therapy

9.2.1 In Vivo Gene Therapy Market Trends Analysis (2021-2032)

9.2.2 In Vivo Gene Therapy Market Size Estimates and Forecasts to 2032 (USD Billion)

9.3 Ex Vivo Gene Therapy

9.3.1 Ex Vivo Gene Therapy Market Trends Analysis (2021-2032)

9.3.2 Ex Vivo Gene Therapy Market Size Estimates and Forecasts to 2032 (USD Billion)

9.4 Others (In-situ Gene therapy)

9.4.1 Others (In-situ Gene therapy) Market Trends Analysis (2021-2032)

9.4.2 Others (In-situ Gene therapy) Market Size Estimates and Forecasts to 2032 (USD Billion)

10. Gene Therapy Platform Market Segmentation By End-User

10.1 Chapter Overview

10.2 Pharmaceutical & Biotechnology Companies

10.2.1 Pharmaceutical & Biotechnology Companies Market Trends Analysis (2021-2032)

10.2.2 Pharmaceutical & Biotechnology Companies Market Size Estimates and Forecasts to 2032 (USD Billion)

10.3 Academic & Research Institutions

10.3.1 Academic & Research Institutions Market Trend Analysis (2021-2032)

10.3.2 Academic & Research Institutions Market Size Estimates and Forecasts to 2032 (USD Billion)

10.4 Contract Development & Manufacturing Organizations (CDMOs)

10.4.1 Contract Development & Manufacturing Organizations (CDMOs) Market Trends Analysis (2021-2032)

10.4.2 Contract Development & Manufacturing Organizations (CDMOs) Market Size Estimates and Forecasts to 2032 (USD Billion)

10.5 Hospitals & Gene Therapy Centers

10.5.1 Hospitals & Gene Therapy Centers Market Trends Analysis (2021-2032)

10.5.2 Hospitals & Gene Therapy Centers Market Size Estimates and Forecasts to 2032 (USD Billion)

11. Regional Analysis

11.1 Chapter Overview

11.2 North America

11.2.1 Trend Analysis

11.2.2 North America Gene Therapy Platform Market Estimates and Forecasts by Country (2021-2032) (USD Billion)

11.2.3 North America Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion) 

11.2.4 North America Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.2.5 North America Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.2.6 North America Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.2.7 USA

11.2.7.1 USA Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.2.7.2 USA Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.2.7.3 USA Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.2.7.4 USA Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.2.8 Canada

11.2.8.1 Canada Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.2.8.2 Canada Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.2.8.3 Canada Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.2.8.4 Canada Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.2.9 Mexico

11.2.9.1 Mexico Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.2.9.2 Mexico Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.2.9.3 Mexico Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.2.9.4 Mexico Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3 Europe

11.3.1 Trend Analysis

11.3.2 Europe Gene Therapy Platform Market Estimates and Forecasts by Country (2021-2032) (USD Billion)

11.3.3 Europe Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion) 

11.3.4 Europe Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.5 Europe Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.6 Europe Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.7 Germany

11.3.7.1 Germany Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.7.2 Germany Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.7.3 Germany Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.7.4 Germany Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.8 France

11.3.8.1 France Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.8.2 France Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.8.3 France Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.8.4 France Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.9 UK

11.3.9.1 UK Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.9.2 UK Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.9.3 UK Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.9.4 UK Gene Therapy Platform Market Estimates and Forecasts by End-User  (2021-2032) (USD Billion)

11.3.10 Italy

11.3.10.1 ItalyGene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.10.2 Italy Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.10.3 Italy Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.10.4 Italy Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.11 Spain

11.3.11.1 Spain Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.11.2 Spain Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.11.3 Spain Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.11.4 Spain Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.12 Poland

11.3.12.1 Poland Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.12.2 Poland Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.12.3 Poland Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.12.4 Poland Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.13 Turkey

11.3.13.1 Turkey Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.13.2 Turkey Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.13.3 Turkey Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.13.4 Turkey Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.3.14 Rest of Europe

11.3.14.1 Rest of Europe Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.3.14.2 Rest of Europe Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.3.14.3 Rest of Europe Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.3.14.4 Rest of Europe Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4 Asia Pacific

11.4.1 Trend Analysis

11.4.2 Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Country (2021-2032) (USD Billion)

11.4.3 Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion) 

11.4.4 Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.5 Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.6 Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.7 China

11.4.7.1 China Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.7.2 China Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.7.3 China Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.7.4 China Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.8 India

11.4.8.1 India Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.8.2 India Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.8.3 India Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.8.4 India Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.9 Japan

11.4.9.1 Japan Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.9.2 Japan Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.9.3 Japan Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.9.4 Japan Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.10 South Korea

11.4.10.1 South Korea Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.10.2 South Korea Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.10.3 South Korea Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.10.4 South Korea Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.11 Singapore

11.4.11.1 Singapore Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.11.2 Singapore Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.11.3 Singapore Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.11.4 Singapore Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.12 Australia

11.4.12.1 Australia Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.12.2 Australia Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.12.3 Australia Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.12.4 Australia Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.4.13 Rest of Asia Pacific

11.4.13.1 Rest of Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.4.13.2 Rest of Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.4.13.3 Rest of Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.4.13.4 Rest of Asia Pacific Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.5 Middle East and Africa

11.5.1 Trend Analysis

11.5.2 Middle East and Africa Gene Therapy Platform Market Estimates and Forecasts by Country (2021-2032) (USD Billion)

11.5.3 Middle East and Africa Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion) 

11.5.4 Middle East and Africa Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.5.5 Middle East and Africa Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.5.6 Middle East and Africa Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.5.7 UAE

11.5.7.1 UAE Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.5.7.2 UAE Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.5.7.3 UAE Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.5.7.4 UAE Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.5.8 Saudi Arabia

11.5.8.1 Saudi Arabia Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.5.8.2 Saudi Arabia Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.5.8.3 Saudi Arabia Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.5.8.4 Saudi Arabia Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.5.9 Qatar

                     11.5.9.1 Qatar Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.5.9.2 Qatar Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.5.9.3 Qatar Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.5.1.9.4 Qatar Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.5.10   South Africa

11.5.10.1 South Africa Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.5.10.2 South Africa Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.5.10.3 South Africa Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.5.10.4 South Africa Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.5.11 Rest of Middle East & Africa

                    11.5.11.1 Rest of Middle East & Africa Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.5.11.2 Rest of Middle East & Africa  Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.5.11.3 Rest of Middle East & Africa Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.5.11.4 Rest of Middle East & Africa Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.6 Latin America

11.6.1 Trend Analysis

11.6.2 Latin America Gene Therapy Platform Market Estimates and Forecasts by Country (2021-2032) (USD Billion)

11.6.3 Latin America Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion) 

11.6.4 Latin America Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.6.5 Latin America Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.6.6 Latin America Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.6.7 Brazil

11.6.7.1 Brazil Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.6.7.2 Brazil Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.6.7.3 Brazil Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.6.7.4 Brazil Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.6.8 Argentina

11.6.8.1 Argentina Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.6.8.2 Argentina Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.6.8.3 Argentina Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.6.8.4 Argentina Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

11.6.9 Rest of Latin America

11.6.9.1 Rest of Latin America Gene Therapy Platform Market Estimates and Forecasts by Type (2021-2032) (USD Billion)

11.6.9.2 Rest of Latin America Gene Therapy Platform Market Estimates and Forecasts by Application (2021-2032) (USD Billion)

11.6.9.3 Rest of Latin America Gene Therapy Platform Market Estimates and Forecasts by Delivery Mode (2021-2032) (USD Billion)

11.6.9.4 Rest of Latin America Gene Therapy Platform Market Estimates and Forecasts by End-User (2021-2032) (USD Billion)

12. Company Profiles

12.1 Gene Therapy Platform Companies

          12.1.1 Company Overview

12.1.2 Financial

12.1.3 Products/ Services Offered

12.1.4 SWOT Analysis

12.2 Novartis AG,

           12.2.1 Company Overview

12.2.2 Financial

12.2.3 Products/ Services Offered

12.2.4 SWOT Analysis

12.3 Gilead Sciences Inc. (Kite Pharma)           

          12.3.1 Company Overview

12.3.2 Financial

12.3.3 Products/ Services Offered

12.3.4 SWOT Analysis

12.4 Spark Therapeutics Inc. (a Roche company)

          12.4.1 Company Overview

12.4.2 Financial

12.4.3 Products/ Services Offered

12.4.4 SWOT Analysis

12.5 Bluebird bio Inc.,

          12.5.1 Company Overview

12.5.2 Financial

12.5.3 Products/ Services Offered

12.5.4 SWOT Analysis

12.6 REGENXBIO Inc.,

            12.6.1 Company Overview

12.6.2 Financial

12.6.3 Products/ Services Offered

12.6.4 SWOT Analysis

12.7 Sarepta Therapeutics Inc.,

          12.7.1 Company Overview

12.7.2 Financial

12.7.3 Products/ Services Offered

12.7.4 SWOT Analysis

12.8 uniQure N.V.,

12.8.1 Company Overview

12.8.2 Financial

12.8.3 Products/ Services Offered

12.8.4 SWOT Analysis

12.9 Audentes Therapeutics Inc. (Astellas),

12.9.1 Company Overview

12.9.2 Financial

12.9.3 Products/ Services Offered

12.9.4 SWOT Analysis

12.10 Amicus Therapeutics Inc.

12.10.1 Company Overview

12.10.2 Financial

12.10.3 Products/ Services Offered

12.10.4 SWOT Analysis

13. Use Cases and Best Practices

14. Conclusion